Michelle A Farrar

MBBS (Hons), FRACP, PhD, Associate Professor of Paediatric Neurology, School of Women’s and Children’s Health, UNSW Medicine, UNSW Sydney and Department of Neurology, Sydney Children’s Hospital Network, Sydney, NSW

Ethical aspects of the changing landscape for spinal muscular atrophy management in Australia

New methods of detecting and treating spinal muscular atrophy can be increasingly complex to navigate for both healthcare professionals and at-risk families.

The changing therapeutic landscape of spinal muscular atrophy

What was once a fatal disease at the severe end of the spectrum is becoming a treatable condition with improved functional status and outcomes.